From: Assessment of the feasibility of exon 45–55 multiexon skipping for duchenne muscular dystrophy
Used AONs | Exon 45–55 skip | NT | Other skips | NT |
---|---|---|---|---|
Exon 45 & 55 (mix) | 4/6 | 4/6 | Exon 45–54 skip (1×) | |
3/6 | 1/6 | |||
Exon 45 & 55 (linked) | 1/6 | 4/6 | ||
6/6 | 6/6 | |||
Exon 45, 46, 47, 48, 49, 50, 51, 52, 53, 54 & 55 | 0/6 | 4/6 | Exon 45–54 skip (1×) | |
6/6 | 6/6 |