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Table 2 Overview of the results for the exon 45–55 multiexon skipping experiments in deletion exon 46–50 cell cultures

From: Assessment of the feasibility of exon 45–55 multiexon skipping for duchenne muscular dystrophy

Used AONs

Exon 45–55 skip

NT

Other skips

NT

Exon 45 & 55 (mix)

4/6

4/6

 

Exon 45–54 skip (1×)

 

3/6

1/6

  

Exon 45 & 55 (linked)

1/6

4/6

  
 

6/6

6/6

  

Exon 45, 46, 47, 48, 49, 50, 51, 52, 53, 54 & 55

0/6

4/6

Exon 45–54 skip (1×)

 
 

6/6

6/6